Estudio de fase 3 multicéntrico, de etiqueta abierta para evaluar la eficacia, farmacocinética, seguridad e inmunogenicidad del ustekinumab administrado porvía subcutánea en participantes pediátricos con artritis psoriásica juvenil activa(PSUMMIT Jr)

• Protocol code: CNTO1275JPA3001
• EudraCT code: 2020-005503-40
• Research group: Rheumatology
• Service: Internal Medicine
• Principal investigator:  Lopez Corbeto, Mireia
• Phase: Fase III

Estudio multicéntrico y abierto para evaluar la seguridad, la tolerabilidad, la farmacocinética y el efecto sobre las convulsiones y los síntomas conductuales del radiprodil en pacientes con complejo de esclerosis tuberosa (CET) o displasia cortical focal (DCF) tipo II

• Protocol code: RAD-GRIN-201
• EudraCT code: No aplica
• Research group: Research Group on Status Epilepticus and Acute Seizures
• Service: Neurology
• Principal investigator:  Toledo Argany, Manuel
• Pathology: Malalties del sistema nerviós
• Phase: Fase I

A randomised, double-blind, placebo-controlled, parallel group trial evaluating safety, tolerability, pharmacodynamics and pharmacokinetics of BI 1291583 one tablet once daily over 12 weeks versus placebo in adult patients with cystic fibrosis bronchiectasis (ClairaflyTM)

• Protocol code: 1397-0013
• EudraCT code: No aplica
• Research group: Pneumology
• Service: Pneumology
• Principal investigator:  Álvarez Fernandez, Antonio
• Pathology: Malalties del sistema respiratori
• Phase: Fase II

Estudio de seguimiento a largo plazo de pacientes con MPS IIIA procedentes de ensayos clínicos de terapia génica que incluyen la administración de ABO-102 (scAAV9.U1a.hSGSH)

• Protocol code: LTFU-ABO-102
• EudraCT code: 2019-002979-34
• Research group: Pediatric Neurology
• Service: General Pediatrics and Specialties
• Principal investigator:  Toro Riera, Mireia del
• Pathology: Malalties del sistema nerviós
• Phase: Fase III

A phase 3, multicentre, randomised, double-blind, vehicle-controlled, parallel-group study to evaluate, the efficacy and safety of tribanulib 10 mg, ointment applied to a treatment, field larger than 25 cm and up to 10 cm in adult patients with actinic keratosis.

• Protocol code: M-14867-33
• EudraCT code: No aplica
• Research group: Biomedical Research in Melanoma
• Service: Dermatologia
• Principal investigator:  Ferrándiz Pulido, Carla
• Pathology: Tumors
• Phase: Fase III
• Status: Recruiting volunteers

A study evaluating the safety and efficacy of once-weekly dosing of somapacitan in a basket study design in paediatric participants with short stature either born small for gestational age or with Turner syndrome, Noonan syndrome or idiopathic short stature.

• Protocol code: NN8640-4469
• EudraCT code: No aplica
• Research group: Growth and Development
• Service: General Pediatrics and Specialties
• Principal investigator:  Mogas Viñas, Eduard
• Pathology: Certes afeccions originades en el període perinatal
• Phase: Fase III
• Status: Recruiting volunteers